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PNH - Paroxysmal Nocturnal Hemoglobinuria

1
Pipeline Programs
2
Companies
2
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
1
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Longbio Pharma
Longbio PharmaChina - Shanghai
1 program
1
LP-005 InjectionPhase 21 trial
Active Trials
NCT07212426Active Not Recruiting30Est. Mar 2028
NovelMed Therapeutics
NovelMed TherapeuticsOH - Cleveland
1 program
NM8074PHASE_21 trial
Active Trials
NCT05731050Not Yet Recruiting6Est. Mar 2028

Trial Timeline

Clinical trial activity over time

2024
2025
2026
2027
2028
NovelMed TherapeuticsNM8074
Longbio PharmaLP-005 Injection

Clinical Trials (2)

Total enrollment: 36 patients across 2 trials

Study of NM8074 in Soliris-Treated Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Start: Jun 2026Est. completion: Mar 20286 patients
Phase 2Not Yet Recruiting

Efficacy, Safety, and Pharmacokinetics of LP-005 Injection in PNH Patients.

Start: Nov 2024Est. completion: Mar 202830 patients
Phase 2Active Not Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

2 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.