Pantothenate Kinase-Associated Neurodegeneration
1
Pipeline Programs
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Companies
1
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
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Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Travere TherapeuticsFosmetpantotenate
Clinical Trials (1)
Total enrollment: 84 patients across 1 trials
Efficacy and Safety Study of Fosmetpantotenate (RE-024) in PKAN Participants
Start: Jul 2017Est. completion: Dec 201984 patients
Phase 3Terminated
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 late-stage (Phase 3) programs — potential near-term approvals
1 companies competing in this space