Noonan Syndrome

1
Pipeline Programs
2
Companies
2
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
1
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Insmed
InsmedBRIDGEWATER, NJ
1 program
1
rhIGF-1/rhIGFBP-3Phase 21 trial
Active Trials
NCT00351221Terminated24
Novo Nordisk
Novo NordiskBAGSVAERD DENMARK, Denmark
1 program
NorditropinN/A1 trial
Active Trials
NCT05308927Enrolling By Invitation221Est. Mar 2028

Trial Timeline

Clinical trial activity over time

2022
2023
2024
2025
2026
2027
2028
Novo NordiskNorditropin

Clinical Trials (2)

Total enrollment: 245 patients across 2 trials

NCT00351221InsmedrhIGF-1/rhIGFBP-3

Research Study Using Recombinant Human Insulin-Like Growth Factor-1/Recombinant Human Insulin-Like Growth Factor Binding Protein-3 for Children With Noonan Syndrome

24 patients
Phase 2Terminated

French Registry of Children Treated With Norditropin® for Short Stature Associated With Noonan Syndrome

Start: Mar 2022Est. completion: Mar 2028221 patients
N/AEnrolling By Invitation

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

2 companies competing in this space