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NF1

2
Pipeline Programs
4
Companies
3
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
1
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
1100%
+ 3 programs with unclassified modality

Competitive Landscape

4 companies ranked by most advanced pipeline stage

Angeles Therapeutics
Angeles TherapeuticsCA - Los Angeles
1 program
1
Poly ICLCPhase 21 trial
Active Trials
NCT04544007Terminated3Est. Nov 2024
Amgen
AmgenTHOUSAND OAKS, CA
1 program
1
ImlygicPhase 11 trial
Active Trials
NCT07102394Recruiting10Est. Dec 2027
Medtronic
MedtronicNJ - Phillipsburg
1 program
INFUSE Bone GraftN/A1 trial
Active Trials
NCT02718131Terminated5Est. Jun 2020
SpringWorks Therapeutics
1 program
MirdametinibPHASE_1_2Small Molecule

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
Angeles TherapeuticsPoly ICLC
AmgenImlygic
MedtronicINFUSE Bone Graft

Clinical Trials (3)

Total enrollment: 18 patients across 3 trials

A Phase II Trial of Poly-ICLC for Low-Grade Gliomas

Start: Feb 2022Est. completion: Nov 20243 patients
Phase 2Terminated

Feasibility and Tolerability of IMLYGIC for the Treatment of Cutaneous Neurofibromas in Adults With NF1

Start: Feb 2026Est. completion: Dec 202710 patients
Phase 1Recruiting
NCT02718131MedtronicINFUSE Bone Graft

A Study of INFUSE Bone Graft (BMP-2) in the Treatment of Tibial Pseudarthrosis in Neurofibromatosis Type 1 (NF1)

Start: Mar 2016Est. completion: Jun 20205 patients
N/ATerminated

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 18 patients
4 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.