Neuromuscular Disease
0
Pipeline Programs
3
Companies
2
Clinical Trials
1 recruiting
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
3 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
2027
2028
Regeneronnexiguran ziclumeran
ResMedincrease of cough peak flow
Clinical Trials (2)
Total enrollment: 80 patients across 2 trials
A Phase 3 Study of NTLA-2001 in ATTRv-PN
Start: Nov 2024Est. completion: Aug 202860 patients
Phase 3Recruiting
Comparison of a Hyperinflation Mode and Air Stacking on Neuromuscular Patients Under Volumetric Ventilation
Start: Sep 2016Est. completion: Mar 201720 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 actively recruiting trials targeting 80 patients
3 companies competing in this space
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