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Neurofibromatosis Type 1-Associated Plexiform Neurofibromas

0
Pipeline Programs
2
Companies
6
Clinical Trials
4 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
2100%

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Merck & Co.
Merck & Co.RAHWAY, NJ
1 program
MirdametinibN/ASmall Molecule5 trials
Active Trials
NCT05028166Available
NCT07539441Recruiting26Est. Oct 2029
NCT06843967Recruiting54Est. Aug 2028
+2 more trials
SpringWorks Therapeutics
1 program
MirdametinibN/ASmall Molecule

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
Merck & Co.Mirdametinib
Merck & Co.Mirdametinib
Merck & Co.Mirdametinib
Merck & Co.Mirdametinib
Merck & Co.Mirdametinib

Clinical Trials (6)

Total enrollment: 259 patients across 6 trials

A Study of Mirdametinib in People With Central Nervous System Tumors

Start: Apr 2026Est. completion: Oct 202926 patients
Phase 1/2Recruiting

A Study of Mirdametinib in Combination With Palbociclib in People With Liposarcoma

Start: Feb 2025Est. completion: Aug 202854 patients
Phase 1/2Recruiting

Mirdametinib Monotherapy in Adults With Neurofibromatosis 1 (NF1) and Cutaneous Neurofibromas (cNF).

Start: Feb 2024Est. completion: Nov 202824 patients
Phase 1/2Recruiting

Mirdametinib + BGB-3245 in Advanced Solid Tumors

Start: Feb 2023Est. completion: Jan 202523 patients
Phase 1/2Terminated

SJ901: Evaluation of Mirdametinib in Children, Adolescents, and Young Adults With Low-Grade Glioma

Start: Jun 2021Est. completion: Jun 2031132 patients
Phase 1/2Recruiting

Individual Patient Compassionate Use of Mirdametinib

N/AAvailable

Phase Legend

Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available

Key Insights

4 actively recruiting trials targeting 259 patients
2 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.