Myoclonus Epilepsies, Progressive

1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Autifony Therapeutics
Autifony TherapeuticsUK - Stevenage
1 program
1
AUT00201Phase 11 trial
Active Trials
NCT05873062Completed6Est. May 2024

Trial Timeline

Clinical trial activity over time

2023
2024
2025
2026
Autifony TherapeuticsAUT00201

Clinical Trials (1)

Total enrollment: 6 patients across 1 trials

Safety, Blood Levels and Effects of AUT00201 in Patients With MEAK

Start: May 2023Est. completion: May 20246 patients
Phase 1Completed

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 companies competing in this space