Mucopolysaccharidosis Type 3 B

1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Abeona Therapeutics
Abeona TherapeuticsCLEVELAND, OH
1 program
1
rAAV9.CMV.hNAGLUPhase 1/21 trial
Active Trials
NCT03315182TerminatedEst. Apr 2022

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Abeona TherapeuticsrAAV9.CMV.hNAGLU

Clinical Trials (1)

Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB

Start: Oct 2017Est. completion: Apr 2022
Phase 1/2Terminated

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 companies competing in this space