Mucopolysaccharidosis IV
0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
BioMarin PharmaceuticalNOVATO, CA
1 programDynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVaN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
BioMarin PharmaceuticalDynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa
Clinical Trials (1)
NCT02153255BioMarin PharmaceuticalDynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa
Dynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa
Start: Jul 2016Est. completion: Jul 20160
N/AWithdrawn
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space