MPS IVA

0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

BioMarin Pharmaceutical
1 program
Gait Analysis in MPS IVAN/A1 trial
Active Trials
NCT01920828Completed10Est. Jun 2017

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
BioMarin PharmaceuticalGait Analysis in MPS IVA

Clinical Trials (1)

Total enrollment: 10 patients across 1 trials

NCT01920828BioMarin PharmaceuticalGait Analysis in MPS IVA

Gait Analysis in MPS IVA

Start: Aug 2013Est. completion: Jun 201710 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 companies competing in this space