Long Chain Fatty Acid Oxidation Disorders

0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Ultragenyx Pharmaceutical
1 program
TriheptanoinN/A1 trial
Active Trials
NCT03773770Available

Clinical Trials (1)

NCT03773770Ultragenyx PharmaceuticalTriheptanoin

Expanded Access to Triheptanoin

N/AAvailable

Phase Legend

Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available

Key Insights

1 companies competing in this space