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Leukodystrophy

0
Pipeline Programs
19
Companies
2
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
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Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

19 companies ranked by most advanced pipeline stage

Passage Bio
Passage BioPA - Philadelphia
1 program
The Myelin Disorders Biorepository ProjectN/A
Orchard Therapeutics
1 program
The Myelin Disorders Biorepository ProjectN/A
ME Therapeutics
ME TherapeuticsNEW YORK, NY
1 program
The Myelin Disorders Biorepository ProjectN/A
Ionis Pharmaceuticals
1 program
The Myelin Disorders Biorepository ProjectN/A
Biogen
BiogenCAMBRIDGE, MA
1 program
The Myelin Disorders Biorepository ProjectN/A
Sana Biotechnology
Sana BiotechnologyWA - Seattle
1 program
The Myelin Disorders Biorepository ProjectN/A
Boehringer Ingelheim
Boehringer IngelheimINGELHEIM, Germany
1 program
The Myelin Disorders Biorepository ProjectN/A
Eli Lilly and Company
Eli Lilly and CompanyINDIANAPOLIS, IN
1 program
The Myelin Disorders Biorepository ProjectN/A
United Therapeutics
United TherapeuticsMD - Silver Spring
1 program
The Myelin Disorders Biorepository ProjectN/A
BioTherapeutics Inc
BioTherapeutics IncVA - Blacksburg
1 program
The Myelin Disorders Biorepository ProjectN/A
Sana Health
Sana HealthCO - Louisville
1 program
The Myelin Disorders Biorepository ProjectN/A
Takeda
TakedaTOKYO, Japan
1 program
The Myelin Disorders Biorepository ProjectN/A
Bio-Me
Bio-MeNorway - Oslo
1 program
The Myelin Disorders Biorepository ProjectN/A
MSD
MSDIreland - Ballydine
1 program
The Myelin Disorders Biorepository ProjectN/A
Biocorp
BiocorpFrance - Issoire
1 program
The Myelin Disorders Biorepository ProjectN/A
Prevail Therapeutics
1 program
The Myelin Disorders Biorepository ProjectN/A1 trial
Active Trials
NCT03047369Recruiting12,000Est. Dec 2030
Myrtelle
MyrtelleMA - Wakefield
1 program
The Myelin Disorders Biorepository ProjectN/A
Human BioSciences
Human BioSciencesWV - Martinsburg
1 program
The Nosology and Etiology of Leukodystrophies of Unknown CausesN/A1 trial
Active Trials
NCT00889174Completed76Est. Aug 2018
Genome & Company
Genome & CompanyKorea - Suwon
1 program
The Nosology and Etiology of Leukodystrophies of Unknown CausesN/A

Trial Timeline

Clinical trial activity over time

2021
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2029
2030
Prevail TherapeuticsThe Myelin Disorders Biorepository Project
Human BioSciencesThe Nosology and Etiology of Leukodystrophies of Unknown Causes

Clinical Trials (2)

Total enrollment: 12,076 patients across 2 trials

NCT03047369Prevail TherapeuticsThe Myelin Disorders Biorepository Project

The Myelin Disorders Biorepository Project

Start: Dec 2016Est. completion: Dec 203012,000 patients
N/ARecruiting
NCT00889174Human BioSciencesThe Nosology and Etiology of Leukodystrophies of Unknown Causes

The Nosology and Etiology of Leukodystrophies of Unknown Causes

Start: Apr 2009Est. completion: Aug 201876 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 12,076 patients
19 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.