Leber's Congenital Amaurosis
1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products
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Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
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Early DiscoveryClinical DevelopmentMarket
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Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Thea PharmaQR-110
Clinical Trials (1)
Study to Evaluate QR-110 in Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene
Start: Oct 2017Est. completion: Oct 2019
Phase 1/2Completed
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
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