Lafora Disease
0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Ionis PharmaceuticalsCARLSBAD, CA
1 programNatural History and Functional Status Study of Patients With Lafora DiseaseN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Ionis PharmaceuticalsNatural History and Functional Status Study of Patients With Lafora Disease
Clinical Trials (1)
Total enrollment: 33 patients across 1 trials
NCT03876522Ionis PharmaceuticalsNatural History and Functional Status Study of Patients With Lafora Disease
Natural History and Functional Status Study of Patients With Lafora Disease
Start: Jan 2019Est. completion: Apr 202233 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space