Iron Overload
1
Pipeline Programs
2
Companies
3
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
1
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
2 companies ranked by most advanced pipeline stage
NovartisBASEL, Switzerland
2 programs1
DesferasiroxPhase 41 trial
Iron Overload in Pediatric Oncology PatientsN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
NovartisDesferasirox
One BiosciencesR2*-UTE
NovartisIron Overload in Pediatric Oncology Patients
Clinical Trials (3)
Total enrollment: 139 patients across 3 trials
Safety and Efficacy of Desferasirox in Chinese Patients With Iron Overload and Aplastic Anemia
Start: Oct 2011Est. completion: Nov 201364 patients
Phase 4Completed
Massive Iron Deposit Assessment
Start: Jun 2012Est. completion: Feb 2018
N/ACompleted
Iron Overload in Pediatric Oncology Patients
Start: Dec 2009Est. completion: Jan 201275 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
2 companies competing in this space