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Hemophagocytic Lymphohistiocytosis

2
Pipeline Programs
4
Companies
5
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
0
0
1
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Monoclonal Antibody
150%
Small Molecule
150%
+ 3 programs with unclassified modality

Competitive Landscape

4 companies ranked by most advanced pipeline stage

Eppendorf
EppendorfGermany - Hamburg
1 program
1
DexamethasonePhase 31 trial
Active Trials
NCT00426101Completed368Est. Dec 2017
Incyte
IncyteDE - Wilmington
1 program
1
RuxolitinibPhase 1/2Small Molecule1 trial
Active Trials
NCT04551131Active Not Recruiting10Est. Aug 2026
Swedish Orphan Biovitrum
2 programs
Blood DrawsN/A1 trial
EmapalumabPHASE_2_3Monoclonal Antibody1 trial
Active Trials
NCT03259230Completed40Est. Jan 2020
NCT02069899Completed58Est. May 2021
Chia Tai TianQing Pharmaceutical Group
1 program
TQ05105PHASE_11 trial
Active Trials
NCT04326348Unknown40Est. Jul 2022

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
EppendorfDexamethasone
Swedish Orphan BiovitrumEmapalumab
IncyteRuxolitinib
Chia Tai TianQing Pharmaceutical GroupTQ05105
Swedish Orphan BiovitrumBlood Draws

Clinical Trials (5)

Total enrollment: 516 patients across 5 trials

Treatment Protocol for Hemophagocytic Lymphohistiocytosis 2004

Start: Jan 2004Est. completion: Dec 2017368 patients
Phase 3Completed

A Study for Long-term Follow-up of Hemophagocytic Lymphohistiocytosis (HLH) Participants Who Received Treatment With Emapalumab (NI-0501), an Anti-interferon Gamma Monoclonal Antibody

Start: Aug 2014Est. completion: May 202158 patients
Phase 2/3Completed

Use Of A Response-Adapted Ruxolitinib-Containing Regimen For The Treatment Of Hemophagocytic Lymphohistiocytosis

Start: Jul 2021Est. completion: Aug 202610 patients
Phase 1/2Active Not Recruiting

A Study of TQ05105 Tablets in Subjects With Hemophagocytic Lymphohistiocytosis(HLH)

Start: Jul 2020Est. completion: Jul 202240 patients
Phase 1Unknown

Evaluation of IFNγ and Inflammatory Mediators in Patients With Malignancy-Associated Hemophagocytic Lymphohistiocytosis

Start: Oct 2016Est. completion: Jan 202040 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs, potential near-term approvals
4 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.