Hemoglobinopathies
1
Pipeline Programs
3
Companies
2
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
1
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
3 companies ranked by most advanced pipeline stage
Heidelberg PharmaGermany - Ladenburg
1 programNon applicable, is a patient registryN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Sandozdeferasirox
Heidelberg PharmaNon applicable, is a patient registry
Clinical Trials (2)
Total enrollment: 802 patients across 2 trials
Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload
Start: Nov 2007Est. completion: Sep 2011118 patients
Phase 4Completed
ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19
Start: Apr 2020Est. completion: Dec 2023684 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
3 companies competing in this space
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