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Hematologic Malignancies

23
Pipeline Programs
28
Companies
50
Clinical Trials
10 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
10
0
11
1
1
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
556%
Cell Therapy
222%
Monoclonal Antibody
222%
+ 34 programs with unclassified modality

Competitive Landscape

28 companies ranked by most advanced pipeline stage

Pfizer
PfizerNEW YORK, NY
5 programs
2
2
1
piperacillin/tazobactamPhase 35 trials
AnidulafunginPhase 21 trial
extracorporeal photopheresisPhase 21 trial
PF-04449913Phase 11 trial
PF-0791800Phase 11 trial
Active Trials
NCT00953758Completed47Est. Feb 2013
NCT02663518Terminated249Est. Nov 2022
NCT01053884Terminated10Est. Sep 2011
+6 more trials
Gamida Cell
Gamida CellIsrael - Kiryat Gat
2 programs
1
1
StemEx®Phase 2/31 trial
StemExPhase 21 trial
Active Trials
NCT01484470Completed18Est. Nov 2018
NCT00469729Completed101Est. Jun 2015
Incyte
IncyteDE - Wilmington
3 programs
1
2
CyclophosphamidePhase 21 trial
TafasitamabPhase 2Monoclonal Antibody1 trial
ItacitinibPhase 1Small Molecule1 trial
Active Trials
NCT03320642Terminated84Est. Feb 2022
NCT07359859Recruiting40Est. Jan 2029
NCT06465433Recruiting25Est. Aug 2027
MSD
MSDIreland - Ballydine
2 programs
2
NemtabrutinibPhase 2Small Molecule1 trial
ridaforolimusPhase 21 trial
Active Trials
NCT04728893Recruiting490Est. Jan 2029
NCT00086125Completed57Est. Jun 2006
Sharp Therapeutics
Sharp TherapeuticsPA - Pittsburgh
2 programs
2
NemtabrutinibPhase 2Small Molecule
ridaforolimusPhase 2
Pulmotect
PulmotectTX - Houston
1 program
1
PUL-042Phase 21 trial
Active Trials
NCT06665100Recruiting100Est. May 2027
Sandoz
SandozAustria - Kundl
1 program
1
ceritinibPhase 2Small Molecule1 trial
Active Trials
NCT02343679Withdrawn0Est. Oct 2022
Angiocrine Bioscience
Angiocrine BioscienceCA - San Diego
1 program
1
AB-110Phase 11 trial
Active Trials
NCT03483324Completed10Est. Jan 2022
Ascentage Pharma
Ascentage PharmaChina - Beijing
1 program
1
APG-2575Phase 11 trial
Active Trials
NCT03537482Recruiting90Est. Feb 2025
SystImmune
SystImmuneWA - Redmond
1 program
1
GNC-035Phase 11 trial
Active Trials
NCT05104775Active Not Recruiting33Est. Dec 2025
Innate Pharma
Innate PharmaFrance - Marseille
1 program
1
MonalizumabPhase 1Monoclonal Antibody1 trial
Active Trials
NCT02921685Unknown18Est. Apr 2020
Healios
HealiosJapan - Tokyo
1 program
1
MultiStem®Phase 11 trial
Active Trials
NCT00677859Completed36Est. Nov 2011
RegeneCore Biotech
RegeneCore BiotechChina - Nanjing
1 program
1
RJK-RT2831 dose-escalation phase IaPhase 11 trial
Active Trials
NCT06756451Recruiting71Est. Jul 2028
Prescient Therapeutics
Prescient TherapeuticsAustralia - South Melbourne
1 program
1
TriciribinePhase 11 trial
Active Trials
NCT00642031Completed20Est. Oct 2012
Fate Therapeutics
Fate TherapeuticsSAN DIEGO, CA
4 programs
Biological: ProHema-CBPHASE_11 trial
FludarabinePHASE_11 trial
ProTmunePHASE_1_21 trial
ProHema-CBPHASE_21 trial
Active Trials
NCT02354417Terminated3Est. Feb 2017
NCT00890500Completed12Est. Oct 2013
NCT02743351Completed96Est. Nov 2021
+1 more trials
Sanofi
SanofiPARIS, France
3 programs
CAMPATHPHASE_15 trials
ClofarabinePHASE_11 trial
clofarabinePHASE_11 trial
Active Trials
NCT01307332Completed27Est. Sep 2018
NCT00914758Unknown1Est. Dec 2011
NCT00836043Terminated6Est. Apr 2009
+4 more trials
Allogene Therapeutics
Allogene TherapeuticsSOUTH SAN FRANCISCO, CA
2 programs
Follow-Up for Study Participants Treated With an Allogeneic CAR T-Cell ProductN/ACell Therapy1 trial
allogeneic CAR T cell therapyN/ACell Therapy
Active Trials
NCT06925685Enrolling By Invitation50Est. Jan 2039
Coordination Pharmaceuticals
1 program
Extensive GAN/A1 trial
Active Trials
NCT02884375Recruiting3,000Est. Nov 2027
Bristol Myers Squibb
1 program
UCB and HPDSCN/A1 trial
Active Trials
NCT00596999Unknown6Est. Dec 2013
Hutchmed
HutchmedChina - Hong Kong
1 program
HMPL-523PHASE_1
IQVIA
IQVIADURHAM, NC
1 program
HMPL-523PHASE_11 trial
Active Trials
NCT02503033Unknown78Est. Mar 2021
Jazz Pharmaceuticals
Jazz PharmaceuticalsCA - Palo Alto
1 program
mPEG-r-crisantaspasePHASE_11 trial
Active Trials
NCT01551524Completed36Est. Feb 2015
Sellas Life Sciences Group
1 program
SLS009PHASE_1_21 trial
Active Trials
NCT04588922Recruiting160Est. Dec 2027
Takeda
TakedaTOKYO, Japan
1 program
Immune Globulin InfusionPHASE_22 trials
Active Trials
NCT05952804Recruiting150Est. Jul 2028
NCT01485796Completed54Est. Jan 2013
Novartis
NovartisBASEL, Switzerland
1 program
ceritinibPHASE_2Small Molecule
Merck & Co.
Merck & Co.RAHWAY, NJ
1 program
ridaforolimusPHASE_2
InnoCare
InnoCareChina - Beijing
1 program
ICP-248PHASE_2_31 trial
Active Trials
NCT06378138Recruiting226Est. Jul 2031
Teva
TevaIsrael - Petach Tikva
1 program
StemEx®PHASE_2_3

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
Pfizerpiperacillin/tazobactam
Pfizerpiperacillin/tazobactam
Pfizerpiperacillin/tazobactam
SanofiCAMPATH
SanofiCAMPATH
InnoCareICP-248
Pfizerpiperacillin/tazobactam
TakedaImmune Globulin Infusion
Gamida CellStemEx®
IncyteCyclophosphamide
PulmotectPUL-042
TakedaImmune Globulin Infusion
IncyteTafasitamab
MSDNemtabrutinib
Sandozceritinib

Showing 15 of 50 trials with date data

Clinical Trials (50)

Total enrollment: 8,278 patients across 50 trials

NCT00044928Pfizerpiperacillin/tazobactam

Study Evaluating Zosyn in Hospitalized Patients With Intra-abdominal Infection

Start: Jul 2002Est. completion: Feb 2004262 patients
Phase 4Completed
NCT00044746Pfizerpiperacillin/tazobactam

Study Evaluating the Safety and Efficacy of Piperacillin/Tazobactam and Ampicillin/Sulbactam in Patients With Diabetic Foot Infections

Start: Oct 2000Est. completion: Jan 2003314 patients
Phase 4Completed
NCT00044759Pfizerpiperacillin/tazobactam

Study Comparing the Safety and Efficacy of Piperacillin/Tazobactam to Cefepime in Patients With Hematologic Malignancy or Lymphoma

Est. completion: Jan 2003
Phase 3Completed

Advanced MRI Measures of Repair in Alemtuzumab Treated Patients

Start: Mar 2011Est. completion: Sep 201827 patients
Phase 3Completed

Efficacy/Safety of Frontline Alemtuzumab (Campath, MabCampath) vs Chlorambucil in Patients With Progressive B-Cell Lymphocytic Leukemia

Start: Jul 2001Est. completion: Jun 2006284 patients
Phase 3Completed

ICP-248 in Combination With Orelabrutinib in Treatment-naïve Chronic Lymphocytic Leukemia/Small Lymphocytic Lymphoma (APEX-03)

Start: May 2024Est. completion: Jul 2031226 patients
Phase 2/3Recruiting
NCT01796717Pfizerpiperacillin/tazobactam

Optimizing Dosing Regimen of Piperacillin/Tazobactam for Nosocomial Pneumonia

Start: Mar 2012Est. completion: Dec 201650 patients
Phase 2/3Unknown
NCT01485796TakedaImmune Globulin Infusion

Tolerability and Safety of IGI, 10% With rHuPH20 in PIDD

Start: Dec 2011Est. completion: Jan 201354 patients
Phase 2/3Completed

Efficacy and Safety Study of StemEx®, to Treat Subjects With High Risk Hematologic Malignancies, Following Myeloablative Therapy

Start: Oct 2007Est. completion: Jun 2015101 patients
Phase 2/3Completed
NCT07359859IncyteCyclophosphamide

A Study of Ruxolitinib for Preventing Graft-Versus-Host Disease in People With a Hematologic Malignancy Who Will Receive a Stem Cell Transplant

Start: Jan 2026Est. completion: Jan 202940 patients
Phase 2Recruiting

PUL-042 Treatment in Patients With Parainfluenza Virus (PIV), Human Metapneumovirus (hMPV) or Respiratory Syncytial Virus (RSV)

Start: Jun 2025Est. completion: May 2027100 patients
Phase 2Recruiting
NCT05952804TakedaImmune Globulin Infusion

IVIG for Infection Prevention After CAR-T-Cell Therapy

Start: Jun 2024Est. completion: Jul 2028150 patients
Phase 2Recruiting

Extension Study to Provide Continued Treatment for Patients With Hematologic Malignancies Previously Enrolled in Studies With Tafasitamab

Start: Nov 2022Est. completion: Aug 202725 patients
Phase 2Recruiting
NCT04728893MSDNemtabrutinib

Efficacy and Safety of Nemtabrutinib (MK-1026) in Participants With Hematologic Malignancies (MK-1026-003)

Start: Apr 2021Est. completion: Jan 2029490 patients
Phase 2Recruiting

Novartis PhII Ceritinib (LDK378) in R/R ALK+ Hem Malignancies

Start: May 2015Est. completion: Oct 20220
Phase 2Withdrawn

The PUMA Trial is a Trial of a Single ProHema Modulated-Cord Blood (CB) Unit as Part of a Double CB Transplant in Patients With Hematologic Malignancies.

Start: Jul 2012Est. completion: May 201762 patients
Phase 2Terminated

Umbilical Cord Transplantation for the Elderly Population

Start: Jan 2010Est. completion: Nov 201818 patients
Phase 2Completed
NCT01053884PfizerAnidulafungin

Anidulafungin in Patients With Hematologic Malignancies

Start: Oct 2009Est. completion: Sep 201110 patients
Phase 2Terminated
NCT00402714Pfizerextracorporeal photopheresis

A Trial of Extracorporeal Photopheresis, Pentostatin, and Total Body Irradiation in Patients Undergoing Reduced Intensity Allogeneic Stem Cell Transplantation for the Treatment of Malignancies

Start: Jul 2006Est. completion: Aug 200914 patients
Phase 2Completed
NCT00086125MSDridaforolimus

Study of AP23573 in Patients With Relapsed or Refractory Hematologic Malignancies (8669-024)(COMPLETED)

Start: Jun 2004Est. completion: Jun 200657 patients
Phase 2Completed

Study of SLS009 (Formerly GFH009) a Potent Highly Selective CDK9 Inhibitor in Patients With Hematologic Malignancies and High-Risk Newly Diagnosed AML

Start: May 2021Est. completion: Dec 2027160 patients
Phase 1/2Recruiting

Study of ProTmune for Allogeneic HCT in Adult Patients With Hematologic Malignancies

Start: Dec 2016Est. completion: Nov 202196 patients
Phase 1/2Completed

Alemtuzumab and CHOP Chemotherapy for Aggressive Histological Peripheral T-Cell Lymphomas

Start: Sep 2006Est. completion: May 201520 patients
Phase 1/2Completed

Rituximab Plus CAMPATH in Patients With Relapsed/Refractory Low-Grade or Follicular, CD20-positive, B-cell NHL

Start: Dec 200349 patients
Phase 1/2Terminated

Phase I/II Study of CAMPATH in Patients With Relapsing or Refractory Non-Hodgkin's Lymphoma

Start: Dec 2002Est. completion: Aug 200561 patients
Phase 1/2Terminated
NCT06756451RegeneCore BiotechRJK-RT2831 dose-escalation phase Ia

This Study is a FIH Study Which is Required to Understand the PK Characteristics, MTD, RP2D and Safety Profile.

Start: Mar 2025Est. completion: Jul 202871 patients
Phase 1Recruiting

A Study of GNC-035, a Tetra-specific Antibody, in Participants With Relapsed/Refractory Hematologic Malignancy

Start: Feb 2022Est. completion: Dec 202533 patients
Phase 1Active Not Recruiting

APG-2575 Study of Safety, Tolerability ,PK/PD in Patients With Hematologic Malignancies

Start: Aug 2018Est. completion: Feb 202590 patients
Phase 1Recruiting

Trial of AB-110 in Adults With Hematologic Malignancies Undergoing Cord Blood Transplantation

Start: Apr 2018Est. completion: Jan 202210 patients
Phase 1Completed

GRAVITAS-119: Itacitinib in Combination With Calcineurin Inhibitor-Based Interventions for the Prophylaxis of Graft-Versus Host Disease

Start: Feb 2018Est. completion: Feb 202284 patients
Phase 1Terminated

Study of a Humanized Antibody Initiated 2 Months After an HLA Matched Allogenic Stem Cell Transplantation

Start: Nov 2016Est. completion: Apr 202018 patients
Phase 1Unknown

A Trial of PF-07901800 (TTI-621) for Patients With Hematologic Malignancies and Selected Solid Tumors

Start: Jan 2016Est. completion: Nov 2022249 patients
Phase 1Terminated

A Study of HMPL-523 in Relapsed or Refractory Hematologic Malignancies

Start: Nov 2015Est. completion: Mar 202178 patients
Phase 1Unknown
NCT02354417Fate TherapeuticsBiological: ProHema-CB

A Phase 1 Trial of a Single ProHema® CB Product for Pediatric Patients With Hematologic Malignancies

Start: Dec 2014Est. completion: Feb 20173 patients
Phase 1Terminated

Phase I Study of mPEG-R-Crisantaspase Given IV

Start: Mar 2012Est. completion: Feb 201536 patients
Phase 1Completed

Safety and Efficacy of ProHema Modulated Umbilical Cord Blood Units in Subjects With Hematologic Malignancies.

Start: Jan 2011Est. completion: Oct 201312 patients
Phase 1Completed

A Study Of PF-04449913 In Select Hematologic Malignancies

Start: Mar 2010Est. completion: Feb 201347 patients
Phase 1Completed

Haploidentical Hematopoietic Stem Cell Transplantation Using A Novel Clofarabine Containing Conditioning Regimen For Patients With Refractory Hematologic Malignancies

Start: Jan 2009Est. completion: Dec 201634 patients
Phase 1Completed

Safety Study of MultiStem® in Patients With Acute Leukemia, Chronic Myeloid Leukemia, or Myelodysplasia

Start: Jul 2008Est. completion: Nov 201136 patients
Phase 1Completed

A Phase I Trial of Myeloablative Conditioning w/ Clofarabine and HD Busulfan for Pts w/ Refractory Heme Malignancies Undergoing Allo PBSCT

Start: May 2007Est. completion: Nov 201018 patients
Phase 1Completed

Triciribine Phosphate Monohydrate (TCN-PM, VD-0002) in Adult Patients With Advanced Hematologic Malignancies

Start: Aug 2006Est. completion: Oct 201220 patients
Phase 1Completed

Subcutaneously Administered CAMPATH in CD52 Expressing Hematologic Malignancies

Start: Dec 2003Est. completion: Sep 200524 patients
Phase 1Terminated
NCT06925685Allogene TherapeuticsFollow-Up for Study Participants Treated With an Allogeneic CAR T-Cell Product

Follow-Up for Study Participants Treated With an Allogeneic CAR T-Cell Product

Start: Jan 2025Est. completion: Jan 203950 patients
N/AEnrolling By Invitation

Elderly CAncer Patient

Start: Sep 2010Est. completion: Nov 20273,000 patients
N/ARecruiting

Comparison of Campath and Rebif Treatment on Cognition in Multiple Sclerosis (MS)

Start: Mar 2009Est. completion: Dec 20111 patients
N/AUnknown

Safety, Effectiveness and Patient Acceptance of the Treatment With MabCampath in Chronic Lymphocytic Leukemia

Start: Oct 2008Est. completion: Apr 20096 patients
N/ATerminated

A Single-arm Safety Study of Transplantation Using Umbilical Cord Blood and Human Placental-derived Stem Cells From Partially Matched Related Donors in Persons With Certain Malignant Blood Diseases and Non-malignant Disorders

Start: May 2007Est. completion: Dec 20136 patients
N/AUnknown
NCT00167960Pfizerpiperacillin/tazobactam

Study Evaluating Vancomycin-Resistant Enterococci in a Hematology Unit

Start: Jan 20051,500 patients
N/ACompleted
NCT00195286Pfizerpiperacillin/tazobactam

Study Evaluating Piperacillin/Tazobactam in Complicated Urinary Infections.

Start: Jun 2004Est. completion: Jul 2007180 patients
N/ACompleted

Compassionate Use of Campath-1H in Treating Patients With Refractory Prolymphocytic Leukemia or Chronic Lymphocytic Leukemia

Start: Jan 2000Est. completion: May 20022 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs, potential near-term approvals
10 actively recruiting trials targeting 8,278 patients
28 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.