Haemophilia

0
Pipeline Programs
2
Companies
5
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Pfizer
PfizerNEW YORK, NY
3 programs
Adherence to Treatment in HemophiliaN/A1 trial
Psychology and Physiotherapy groupN/A1 trial
Trainings applicationN/A1 trial
Active Trials
NCT02191436Unknown200Est. Feb 2016
NCT03529474Completed19Est. Mar 2019
NCT04586101Completed20Est. Dec 2021
Novo Nordisk
Novo NordiskBAGSVAERD DENMARK, Denmark
2 programs
Combining Registry Data in Haemophilia: TARGET HN/A1 trial
No treatment givenN/A1 trial
Active Trials
NCT03264014Completed100Est. Sep 2015
NCT07163260Enrolling By Invitation244Est. Dec 2025

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Novo NordiskNo treatment given
PfizerPsychology and Physiotherapy group
PfizerTrainings application
PfizerAdherence to Treatment in Hemophilia
Novo NordiskCombining Registry Data in Haemophilia: TARGET H

Clinical Trials (5)

Total enrollment: 583 patients across 5 trials

NCT07163260Novo NordiskNo treatment given

Defeat Rare Disease in Asia and Pacific (APAC) DRDA - Haemophilia

Start: Jan 2025Est. completion: Dec 2025244 patients
N/AEnrolling By Invitation
NCT03529474PfizerPsychology and Physiotherapy group

Psychology and Physiotherapy Approach of Chronic Pain in Patients With Hemophilia

Start: Mar 2018Est. completion: Mar 201919 patients
N/ACompleted
NCT04586101PfizerTrainings application

iT-based Sports Therapy Application in Haemophilia

Start: Jan 2018Est. completion: Dec 202120 patients
N/ACompleted
NCT02191436PfizerAdherence to Treatment in Hemophilia

Adherence to Treatment in Hemophilia

Start: May 2015Est. completion: Feb 2016200 patients
N/AUnknown
NCT03264014Novo NordiskCombining Registry Data in Haemophilia: TARGET H

Combining Registry Data in Haemophilia: TARGET H

Start: May 2015Est. completion: Sep 2015100 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

2 companies competing in this space