Facio-Scapulo-Humeral Dystrophy

1
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Arrowhead Pharmaceuticals
1 program
1
ARO-DUX4 for InjectionPhase 1/21 trial
Active Trials
NCT06131983Recruiting60Est. Dec 2026

Trial Timeline

Clinical trial activity over time

2024
2025
2026
Arrowhead PharmaceuticalsARO-DUX4 for Injection

Clinical Trials (1)

Total enrollment: 60 patients across 1 trials

Study of ARO-DUX4 in Adult and Adolescent Patients With Facioscapulohumeral Muscular Dystrophy Type 1

Start: Feb 2024Est. completion: Dec 202660 patients
Phase 1/2Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 60 patients
1 companies competing in this space