Crigler-Najjar Syndrome

1
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
1
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Hansa Biopharma
Hansa BiopharmaSweden - Lund
1 program
1
ImlifidasePhase 21 trial
Active Trials
NCT06518005RecruitingEst. Sep 2030

Trial Timeline

Clinical trial activity over time

2024
2025
2026
2027
2028
2029
2030
Hansa BiopharmaImlifidase

Clinical Trials (1)

Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar Syndrome

Start: Nov 2024Est. completion: Sep 2030
Phase 2Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials
1 companies competing in this space