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Craniopharyngioma, Child

0
Pipeline Programs
3
Companies
2
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
2100%
+ 1 programs with unclassified modality

Competitive Landscape

3 companies ranked by most advanced pipeline stage

Colorado Therapeutics
Colorado TherapeuticsCO - Louisville
1 program
Tumor and Blood SpecimensN/A1 trial
Active Trials
NCT03610906Enrolling By Invitation250Est. Dec 2030
One Biosciences
One BiosciencesFrance - Paris
1 program
TovorafenibPHASE_2Small Molecule
Day One Biopharmaceuticals
1 program
TovorafenibPHASE_2Small Molecule1 trial
Active Trials
NCT05465174Recruiting57Est. Mar 2028

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
Day One BiopharmaceuticalsTovorafenib
Colorado TherapeuticsTumor and Blood Specimens

Clinical Trials (2)

Total enrollment: 307 patients across 2 trials

Tovorafenib for Treatment of Craniopharyngioma in Children and Young Adults

Start: Sep 2022Est. completion: Mar 202857 patients
Phase 2Recruiting
NCT03610906Colorado TherapeuticsTumor and Blood Specimens

Prospective Pilot Study Identifying Clinically Relevant Biological Targets for Medical Therapy

Start: Mar 2019Est. completion: Dec 2030250 patients
N/AEnrolling By Invitation

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 307 patients
Small Molecule is the dominant modality (100% of programs)
3 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.