Ceroid Lipofuscinosis, Neuronal 5
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Pipeline Programs
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Companies
1
Clinical Trials
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Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
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Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
NeurogeneNY - New York
1 programA Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)N/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
NeurogeneA Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)
Clinical Trials (1)
Total enrollment: 37 patients across 1 trials
A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)
Start: Mar 2019Est. completion: May 202437 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space
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