Cerebrotendinous Xanthomatosis (CTX)
0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
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0
0
0
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Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Travere TherapeuticsSAN DIEGO, CA
1 programCerebrotendinous Xanthomatosis (CTX) Prevalence StudyN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Travere TherapeuticsCerebrotendinous Xanthomatosis (CTX) Prevalence Study
Clinical Trials (1)
Total enrollment: 442 patients across 1 trials
Cerebrotendinous Xanthomatosis (CTX) Prevalence Study
Start: Sep 2015Est. completion: Feb 2021442 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space