Blau Syndrome

0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
1100%

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Pfizer
PfizerNEW YORK, NY
1 program
TofacitinibN/ASmall Molecule1 trial
Active Trials
NCT06688838Enrolling By Invitation24Est. Dec 2026

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
PfizerTofacitinib

Clinical Trials (1)

Total enrollment: 24 patients across 1 trials

Effective Treatment of Jak1/3 Inhibitor in Blau Syndrome

Start: Jan 2017Est. completion: Dec 202624 patients
N/AEnrolling By Invitation

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 companies competing in this space