Bardet-Biedl Syndrome 1
1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
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Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2026
2027
2028
2029
2030
2031
Axovia TherapeuticsAXV-101
Clinical Trials (1)
Total enrollment: 12 patients across 1 trials
First-in-Human, Dose Escalation Trial of AXV-101 in BBS1-Related Retinal Degeneration
Start: Feb 2026Est. completion: Feb 203212 patients
Phase 1Not Yet Recruiting
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space