Autosomal Dominant Hypocalcemia Type 1 (ADH1)

1
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
1
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

BridgeBio Pharma
BridgeBio PharmaCA - Palo Alto
1 program
1
EncaleretPhase 2/31 trial
Active Trials
NCT07080385Recruiting28Est. Dec 2030

Trial Timeline

Clinical trial activity over time

2026
2027
2028
2029
2030
BridgeBio PharmaEncaleret

Clinical Trials (1)

Total enrollment: 28 patients across 1 trials

Pharmacokinetics, Efficacy, and Safety of Encaleret in Pediatric Participants With Autosomal Dominant Hypocalcemia Type 1 (ADH1)

Start: Jan 2026Est. completion: Dec 203028 patients
Phase 2/3Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 28 patients
1 companies competing in this space