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Autosomal Dominant Hypocalcemia (ADH)

0
Pipeline Programs
2
Companies
5
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
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0
0
0
0
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Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

BridgeBio Pharma
BridgeBio PharmaCA - Palo Alto
2 programs
EncaleretPHASE_21 trial
EncaleretPHASE_33 trials
Active Trials
NCT04581629Completed13Est. Sep 2023
NCT07805356Recruiting160Est. Jan 2033
NCT05735015Completed13Est. Aug 2025
+1 more trials
Takeda
TakedaTOKYO, Japan
1 program
NPSP795PHASE_21 trial
Active Trials
NCT02204579Completed7Est. May 2015

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
BridgeBio PharmaEncaleret
BridgeBio PharmaEncaleret
BridgeBio PharmaEncaleret
BridgeBio PharmaEncaleret
TakedaNPSP795

Clinical Trials (5)

Total enrollment: 260 patients across 5 trials

Efficacy, Safety, and Tolerability of Encaleret in Participants With Chronic Hypoparathyroidism

Start: Aug 2026Est. completion: Jan 2033160 patients
Phase 3Recruiting

Efficacy and Safety of Encaleret Compared to Standard of Care in Participants With ADH1

Start: Jan 2023Est. completion: Aug 202967 patients
Phase 3Active Not Recruiting

PTH-independent Effects of Encaleret

Start: Sep 2023Est. completion: Aug 202513 patients
Phase 2Completed

Safety, Tolerability, and Efficacy of Encaleret in Participants With Autosomal Dominant Hypocalcemia (ADH) Type 1

Start: Sep 2020Est. completion: Sep 202313 patients
Phase 2Completed

A Study to Determine the Effects of NPSP795 on the Calcium-sensing Receptor in Subjects With Autosomal Dominant Hypocalcemia as Measured by PTH Levels and Blood Calcium Concentrations

Start: Jul 2014Est. completion: May 20157 patients
Phase 2Completed

Phase Legend

Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available

Key Insights

1 actively recruiting trials targeting 260 patients
2 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.