Amyloidosis in Transthyretin (TTR)

1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
1
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

BridgeBio Pharma
BridgeBio PharmaCA - Palo Alto
1 program
1
AcoramidisPhase 31 trial
Active Trials
NCT07116473Not Yet Recruiting250Est. Dec 2037

Trial Timeline

Clinical trial activity over time

2025
2026
2027
2028
2029
2030
2031
BridgeBio PharmaAcoramidis

Clinical Trials (1)

Total enrollment: 250 patients across 1 trials

To Evaluate the Long-term Safety and Tolerability of Acoramidis in Participants With Newly Diagnosed ATTR-CM (ACT-EARLY OLE)

Start: Nov 2025Est. completion: Dec 2037250 patients
Phase 3Not Yet Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 companies competing in this space