Amyloidogenic Transthyretin (ATTR) Amyloidosis

1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Prothena
ProthenaDUBLIN 2, Ireland
1 program
1
PRX004Phase 11 trial
Active Trials
NCT03336580Terminated21Est. Jul 2020

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
ProthenaPRX004

Clinical Trials (1)

Total enrollment: 21 patients across 1 trials

A Study of PRX004 in Subjects With Amyloid Transthyretin (ATTR) Amyloidosis

Start: Apr 2018Est. completion: Jul 202021 patients
Phase 1Terminated

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 companies competing in this space