Pipeline & Clinical Trials
NGGT002
PhenylketonuriasClinical Trials (1)
NCT06332807AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
Phase 1/2NGGT002
PhenylketonuriasClinical Trials (1)
NCT06687733Safety and Efficacy Study of NGGT002 in cPKU Adult Subjects
Phase 1/2Phase 1/2
Clinical Trials (1)
NCT06706427Safety and Efficacy Study of NGGT001 in Bietti Crystalline Corneoretinal Dystrophy Subjects
Phase 1/2Open Jobs (0)
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Interview Prep Quick Facts
Founded: 2024
Portfolio: 3 clinical trials